Repurposing ciclopirox as a pharmacological chaperone in a model of congenital erythropoietic porphyria
Urquiza P, Lain A, Sanz-Parra A, Moreno J, Bernardo-Seisdedos G, Dubus P, Gonzalez E, Gutierrez-de-Juan V, Garcia S, Erana H, San Juan I, Macias I,...